Matthew Alexander, PhD
@mattmuscleguy.bsky.social
Geneticist, Skeletal Muscle, Drug development, Gene therapies. Non-coding RNA, and Zebrafish Aficionado. Lover of all things muscle. All posts are my own. Instagram @thealexanderlab
Lab website: https://www.uab.edu/medicine/peds/research/division-researc
Lab website: https://www.uab.edu/medicine/peds/research/division-researc
Indication was for both ambulatory and non-ambulatory. After the patient deaths they removed the non-ambulatory patients indication and placed a black box warning. E.g The non-ambulatory will likely not get it in the US.
E.gm
November 15, 2025 at 2:28 PM
Indication was for both ambulatory and non-ambulatory. After the patient deaths they removed the non-ambulatory patients indication and placed a black box warning. E.g The non-ambulatory will likely not get it in the US.
I believe it's the first time the organizers are putting this together. Hopefully this will be an annual event!
November 12, 2025 at 9:19 PM
I believe it's the first time the organizers are putting this together. Hopefully this will be an annual event!