- Uniqure disclosed Phase1/2 AMT-130 showing - disease slow by about 80% compared to a natural history
- Roche paied $60M upfront to Ionis 2 pre-clinical assets
- Uniqure disclosed Phase1/2 AMT-130 showing - disease slow by about 80% compared to a natural history
- Roche paied $60M upfront to Ionis 2 pre-clinical assets
- Novartis paid $1B upfront to access PTCT's Phase2 staged silicing modulator
- Sage's GABAA receptor modulator Phase 2 drug failed
- Takeda discontinued its collab with Wave's allele-selective antisense oligonucleotide
- Novartis paid $1B upfront to access PTCT's Phase2 staged silicing modulator
- Sage's GABAA receptor modulator Phase 2 drug failed
- Takeda discontinued its collab with Wave's allele-selective antisense oligonucleotide