Thank you for an incredible discussion on next-gen advocacy in rare disease at #BIO2025. Real change takes all of us – patients, families, regulators, industry – pushing forward together.

#RNAsky #rarediseases

Honored to participate in the PPMD 2025 Advocacy Conference, where patients, families, researchers, and policymakers unite to advance progress for #Duchenne. Advocacy plays a key role in shaping policy, driving research, and improving access to treatments for #rarediseases.

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